There are more than 7,000 rare diseases.
Affecting >3% of the world’s population and ~10% of the U.S. population.
80% of rare diseases stem from genetic origins.
Barriers to care [include] lack of awareness, lengthy diagnostic journeys, limited approved treatment options, access to specialized care, geographic limitations and high treatment costs.
It takes ~5+ years for an accurate rare disease diagnosis. For some ultra-rare diseases, it can take even longer.
For 240+ years Takeda has been putting patients first including people living with rare diseases.
[We] aim to discover and deliver life‑transforming medicines [in] hematology, lysosomal storage disorders (LSD), hereditary angioedema (HAE), transplant, neuroscience, gastrointestinal and inflammation, immune‑mediated and primary immune deficiency, immunology.
Our focus areas: improving the standard of care, accelerating time to diagnosis [and] increasing equitable access to care.
Patients deserve answers and a clear path to diagnosis and care.
We are empowering a brighter future in rare disease.
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C‑ANPROM/INT/NON/0031 January 2026